“ In many ways, our move into rare disease is a natural extension of our deep expertise in neurological science ”
In Conversation
“ This is a tumultuous time where the very fabric of biomedical innovation, and the foundational assumptions we have operated on successfully for a generation, have been… ”
“ Our productivity is typically more than 10 times that of a conventional batch process. ”
“ By valuing these medicines as a cornerstone of healthcare affordability and accessibility, we can ensure the long-term sustainability of the entire system. ”
“ We want to prove that there is a viable business model for making these therapies commercially available. ”
“ To any rare disease patient or family, do not give up. Keep going, and do not take no for an answer ”
“ Without a diverse set of options, many patients would simply be left without access to necessary treatment. ”
“ If we do not stop people from getting cancer in the first place, we will not affect incidence, and if we don't affect incidence, it becomes… ”
“ We hope that in the next two years we will see our T-cell approach enter the market and cause a resurgence in the development of this… ”
“ Our core strength lies in interpretation; turning raw sequencing data into actionable diagnoses, supported by deep genotypic and phenotypic context is what sets us apart. ”
“ Patients are our north star. Everything we do ultimately feeds into that approach. ”
“ My goal, and the FDA goal in general, is to make regulatory expectations so efficient that developers are willing to pursue biosimilars for non-blockbuster biologics. ”
